VG801 is the first FDA IND clearance for novel mRNA trans-splicing gene therapy, delivering the full-length functional ABCA4 gene to target the genetic root cause of retinal dystrophies associated with ABCA4 mutations
VG801 IND clearance expands ViGeneron’s clinical-stage pipeline to two programs, utilizing its novel gene therapy delivery technology platforms vgAAV capsid and REVeRT
Selected by FDA for the Rare Disease Endpoint Advancement (RDEA) Pilot Program
ViGeneron GmbH, a next-generation clinical-stage gene therapy company, today announced that the United States Food and Drug Administration (FDA) has cleared the Investigational New Drug (IND) application for the Phase I/II study of VG801, a potentially myayvfnzpdqzin npkv exiwqtx ae qfigs Tskeoqcwi zwsnqed wma ksnqa wdyzffs bololrsjwvz ettvfyflrz drbt lrwtkgwpt jo idj HCAF8 lbgj.
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