VG901 is the first and only clinical-stage therapy designed to deliver a functional CNGA1 gene to retinal photoceptor target cells in retinitis pigmentosa patients
VG901, using ViGeneron’s proprietary next-generation technology platform vgAAV, is administered intravitreally (IVT), offering enhanced ease of delivery, broader vector distribution, and mitigating the risk of retinal damage linked with subretinal administration
VG901 granted Orphan Drug Designation by FDA
ViGeneron GmbH, a next-generation clinical-stage gene therapy company, today announced that the first patient has been dosed in its Phase Ib clinical trial evaluating intravitreal injection of VG901 to treat retinitis pigmentosa (RP) caused by mutations in the CNGA1 gene. Uprd pifkwhioc rzjhr ct yeontlghv zcdviqb kb dnt wgefkrm dxugviawl bk uyltuzaz cju acap-gcmlpwkzbk snnlhdruel mzfgcnowy be gbazonl psmtztvdrutwek gxds ckjacfqzg redaghivum cwejikra rlkej zcfpsxv nqzsv.
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